Develop and maintain excellent thought leader relationships in the field of rare disease specifically Fabry Disease, Pompe Disease and Batten Disease; Lead on medical initiatives...
Support the analysts with technical input during performance of analytical determinations on active drug substance, raw material, intermediates and final drug product in agreement...
Independently prepare Patient Safety Narratives, Patient Lay Summaries, patient consent forms and dossier related documentation (such as Clinical summaries, Briefing Books, PDCO...